AAVs show particular promise in the treatment of neurological disorders, including Parkinson’s disease, amyotrophic lateral sclerosis (ALS), and aromatic L-amino acid decarboxylase (AADC ...

It is cleared for both children and adults with AADC (aromatic L-amino acid decarboxylase) deficiency, a fatal disease that causes severe disability and suffering from the first months of life.

A wave of support has emerged online for a Thai child diagnosed with Aromatic L-amino acid decarboxylase deficiency (AADC Deficiency), a rare genetic disorder affecting only about 130 people worldwide ...

Once full approval is granted Upstaza (eladocagene exuparvovec) will become the first disease-modifying treatment for AADC (aromatic L-amino acid decarboxylase) deficiency, as well as the first ...