本研究首次在CF大鼠模型中发现自发性肺部定植与肠道-肺轴的潜在联系（CF，Cystic Fibrosis） 囊性纤维化（Cystic Fibrosis, CF）是一种由CFTR基因突变引起的遗传性疾病，导致CFTR蛋白功能障碍。该病影响多个器官系统，特别是在肺部和肠道。在肺部，黏液变得黏稠并 ...

ReCode Therapeutics, a clinical-stage genetic medicines company using tissue-specific delivery to power the next wave of mRNA ...

Learn how to navigate cystic fibrosis care with confidence, from treatments and school plans to building a supportive medical ...

A MIRACLE pill that’s been shown to help with many of the symptoms of cystic fibrosis (CF) has been approved for thousands of UK sufferers. The genetic condition affects over 11,000 people ...

Vertex's products are known as cystic fibrosis transmembrane conductance regulator modulators, or CFTR modulators, and they "fix" the malfunctioning protein made by the CFTR gene. Now the tricky thing ...

Use precise geolocation data and actively scan device characteristics for identification. This is done to store and access information on a device and to provide personalised ads and content, ad and ...

Cystic fibrosis (CF) is a genetic condition that affects the lungs, pancreas and other organs, caused by variations on the cystic fibrosis transmembrane conductance regulator  (CFTR) gene. There are ...

In March 2025, Vertex Pharmaceuticals Incorporated announced a study is to evaluate the safety, and tolerability and efficacy ...

Cystic fibrosis (CF) is a life-threatening autosomal recessive disease affecting over 160,000 people worldwide. CF is caused by loss-of-function mutations in the CF transmembrane conductance regulator ...

Vertex Pharmaceuticals today announced that the New Zealand Medicines and Medical Devices Safety Authority (Medsafe) has granted consent for the expanded use of TRIKAFTA® ...