Letasha (left) and Kristina (center) both have COPA syndrome. Their mother, Betty (right), has the same disease mutation in ...
A new type of bone marrow transplant can cure sickle cell disease with only half of the donor's cell proteins matching, ...
A rare genetic disease that ravages some but spares others has baffled researchers — until now. Researchers found that a ...
A single injection of a healthy gene allowed blind children to recognize objects, shapes, and even read — offering hope for ...
Sickle cell disease (SCD), the most common inherited blood disorder, affects millions worldwide. In the United States alone, ...
Bone marrow transplantation (BMT) can potentially cure sickle cell disease, an inherited and painful blood disorder, but ...
Rather than just curing genetic diseases, it could tweak multiple genes that together alter the risk of conditions like Alzheimer’s disease or diabetes. The authors, led by Julian Savulescu ...
A bone marrow transplant process co-developed by investigators at the Johns Hopkins Kimmel Cancer Center is safe and curative ...
Research led by York University's Faculty of Health reveals how a specific mutation in a protein called TRAF1 can shut down ...
Bluebird Bio will sell itself to private equity firms Carlyle and SK Capital for about $30 million, the company said Friday.
Spinal muscular atrophy (SMA) is a debilitating genetic condition that’s usually fatal by a few years of age. But an ...