That partner, Japan’s Nippon Shinyaku, is handing over $110 million upfront to lead on the commercialization of two gene therapies—RGX-121 for Hunter syndrome and RGX-111 for Hurler syndrome.
In a deal potentially worth $810 million for Regenxbio Inc., Nippon Shinyaku Co. Ltd. is partnering on the U.S. and Asian development and commercialization of iduronate-2-sulfatase enzyme RGX-121 for ...
The company is submitting the Hunter syndrome treatment for U.S ... treats another type of mucopolysaccharidosis called Hurler syndrome. It’s earlier in clinical testing. Regenxbio will lead ...