This case of Menkes disease presented with the uncommon association of bilateral inguinal hernias at the age of 4 months. Further investigation demonstrated classical skeletal and neurological ...
The Food and Drug Administration (FDA) has accepted for review the New Drug Application (NDA) under Priority Review for CUTX-101 (copper histidinate) for the treatment of Menkes disease ...
There is currently no cure of FDA-approved treatment for the disease. STORY HIGHLIGHTS FDA accepted Cyprium Therapeutics' CUTX-101 drug application. CUTX-101 treats Menkes disease, a rare genetic ...
The US Food and Drug Administration (FDA) has accepted for filing and priority review of the new drug application (NDA) for Sentynl Therapeutics' CUTX-101 (copper histidinate) for the treatment of ...