MeiraGTx's financials show $125 million in cash, but additional funding will be needed within the next 12 months. Click for ...

Disruption of photoreceptor cilia has been implicated in a variety of retinal diseases, collectively called retinociliopathies, such as Leber congenital amaurosis and retinopathy of prematurity.

Christian, the doctor told Elizabeth, had a retinal disease called Leber congenital amaurosis (LCA). His vision, already bad, would never significantly improve. Nothing could be done. The boy ...

MeiraGTx (MGTX) announced the U.S. Food and Drug Administration, FDA, has granted the Company Rare Pediatric Disease Designation, RPDD, to its ...

US genetic meds company MeiraGTx Holdings yesterday revealed that the US Food and Drug Administration (FDA) has granted the company Rare Pediatric Disease (RPD) designation to its AAV8-RK-RetGC ...