Affected children are born with café-au-lait spots and sometimes Lisch nodules. During adolescence and young adulthood, more than 19% of affected individuals with NF1 develop cutaneous neurofibromas ...

announced the European Medicines Agency (EMA) has granted orphan designation to their codeveloped selumetinib, for the treatment of neurofibromatosis type 1 (NF1), an incurable genetic condition ...

There is currently no cure or treatment for NF1 that can reverse or prevent most complications. Because of this, medical management of the condition focuses on the early detection of treatable ...

Information about the medication for both patients and physicians can be found on the Koselugo web site, and a MEK inhibitor patient information sheet can be found on the Children’s Tumor Foundation ...

a biopsy may be necessary to confirm the diagnosis of a plexiform neurofibroma. A biopsy involves taking a small sample of ...

Pasithea Therapeutics opens European clinical trial sites and completes initial dosing of cohort 4: Miami Thursday, January 16, 2025, 12:00 Hrs [IST] Pasithea Therapeutics Corp., ...