Scientists report results from a promising new approach to treat the rare neurodegenerative disorder. Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before ...

So there are a, um, number of types in regard to SMA. Um, there are four types. And it based upon, the types of SMA are characterized by your motor development, meaning that how much strength do ...

Currently, treatments for SMA have improved survival and helped to ... has now resolved and issues affecting the optic nerve and brain stem. These are thought to have occurred before Evrysdi ...

The U.S. Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for people living with spinal muscular atrophy (SMA). The new tablet is ...