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生物通
14 天
CRISPR/Cas 系统助力 HIV 基因治疗:高效靶向 CCR5 基因的 gRNA 筛选
敲除 CCR5 基因作为治疗 HIV 感染的一种潜在方法,长期以来一直是研究热点。在此,研究人员分析了此前针对 CCR5 基因的 SpCas9 和 AsCas12a 核酸酶的向导 RNA(guide RNAs,gRNAs),并从中筛选出了最有效的 gRNAs。同时,研究人员还利用生物信息学资源为这两种核酸酶 ...
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