Sinar Daily on MSN7 天
Stem cell transplant curative treatment for Thalassemia
The transplant process begins with a human leukocyte antigen typing blood test to determine donor-recipient compatibility for ...
FDA To Decide On Agios' Request For Expanded Approval Of PYRUKYND In Thalassemia By ...
Agios Pharmaceuticals, Inc. (AGIO), on Wednesday, announced that its supplemental New Drug Application seeking approval for the ...
The American Journal of Managed Care8 天
Gene Therapy Demonstrates High Efficacy in Severe β-Thalassemia
A phase 3 trial highlights betibeglogene autotemcel as a potentially curative gene therapy for severe transfusion-dependent β ...
Dr. Roach: Addressing low iron disorder
Dear Dr. Roach: I am Greek and have thalassemia minor. In general, my red blood cells are much smaller than typical ones, and ...
bdnews242 天
Fire claims lives of four of a family on way to seek treatment for son
Mohaimin Islam Fuad, a 14-year-old, had been battling thalassemia for two years. The progressive nature of the disease, which ...
Monthly Prescribing Reference2 天
Mitapivat Under Review for Alpha- and Beta-Thalassemia
The sNDA is supported by data from the phase 3 ENERGIZE and ENERGIZE-T studies, which evaluated mitapivat vs placebo in patients with NTD and TD alpha- or beta-thalassemia, respectively.
BioPharma Dive4 天
Vertex, startup Orna to partner on gene editing research
The three-year partnership is another example of Vertex’s interest in improving on Casgevy, its CRISPR medicine for sickle ...
Minister calls for premarital testing to combat thalassemia in Pakistan
Housing and Works Minister Mian Riaz Hussain Pirzada on Monday emphasized the need for legislation, awareness, mandatory ...
Vertex turns to Watertown biotech for gene-editing medicines pact
Vertex Pharmaceuticals Inc. will work with a Watertown biotech on new gene-editing therapies for people with sickle cell disease and transfusion-dependent beta thalassemia.