A team at the Centro Nacional de Investigaciones Cardiovasculares (CNIC) has developed an innovative gene-therapy strategy ...

一项由北京协和医院和锦篮基因联合开展的研究，首次聚焦中国健康人群和罕见病患者的AAV9抗体分布。该研究在2022年11月至2024年6月期间，招募了341名参与者，年龄覆盖0至90岁，包括270名健康个体和71名罕见病患者。

A team at CNIC has developed an innovative gene therapy to treat arrhythmogenic right ventricular cardiomyopathy type 5 ...

3月22日，东南大学生命健康高等研究院执行院长、东南大学附属中大医院耳鼻咽喉头颈外科柴人杰教授联合多家单位在 Molecular Therapy （《分子治疗》）上在线发表题为“Combined AAV-mediated specific Gjb2 ...

GeneVentiv Therapeutics, a gene therapy company, today announced it has signed a global licensing agreement with Duke ...

"This will be useful across many disciplines which rely on AAV vectors for gene delivery in basic research. It will also make preclinical gene therapy studies in mice more efficient and ...

The death of a 16-year-old boy taking a gene therapy this month dealt a fresh blow to the Duchenne muscular dystrophy ...

To help improve gene therapy, a multidisciplinary team has generated a comprehensive atlas that researchers can use to select ...