The evolution of cell and gene therapy is reshaping drug discovery, providing new hope for rare diseases and cancer through innovative gene editing approaches.

Most recently approved gene therapy products use an adeno-associated virus (AAV) as their gene delivery vector. For example, Elevidys, a new treatment for paediatric patients with DMD that was ...

The trial was able to elicit more than double the microdystrophin gene in patients after 90 days of treatment.

Amicus Therapeutics has two products in the market that generated more than $528 million in revenue last year.

To ensure they have the materials required for each testing phase, researchers can also rely on off-the-shelf plasmid and viral vector solutions, such as those offered by Charles River as a part of ...

PHC Corporation has signed a Master Collaboration Agreement with CCRM to work together on the development of primary ...

The health care system is simply not fully equipped to handle the anticipated approvals of new gene therapy products, Barrett says. "The upfront cost of these therapies contrasts with chronic care ...

The bill from Sen. Brandon Shippy, R-New Plymouth, would place a moratorium on “human gene therapy products” until July 2035. The bill defines those as products that include nucleic acids, ...

The surging stock price indicates the market's confidence in gene therapy products after the successful launch of products such as Roche/Spark Therapeutics' Luxturna, a gene therapy for a rare ...

TCTMD ® is produced by the Cardiovascular Research Foundation ® (CRF). CRF ® is committed to igniting the next wave of innovation in research and education that will help doctors save and improve the ...

Advanced Therapy Connect is a simplified ordering and reporting process for cell and gene therapy products, the company said. Kroger is cutting about 200 employees across three office sites, and ...

C3i became the first contract development and manufacturing organization (CDMO) for cell and gene therapies in Canada to ...