Contract Pharma4 天
ENCell’s EN001 Granted Orphan Drug Designation by FDA
ENCell’s investigational drug EN001 has been granted Orphan Drug Designation by the FDA for the treatment of ...
Business Wire4 天
ENCell’s EN001 Receives Orphan Drug Designation from the U.S. FDA for Charcot-Marie-Tooth ...
EN001, a novel therapy under development by ENCell, has been granted Orphan Drug Designation by the U.S. FDA for the treatment of Charcot-Marie-Tooth (CMT) disease. Phase 1 clinical trial confirmed ...
Claiborne Progress5 天
TN House of Representatives weekly wrap
By State Rep. Dennis Powers House advances bill to regulate hemp-derived THC products To protect consumer health and safety, a new law seeks to regulate the sale and distribution of hemp-derived ...
Sheffield researchers help identify genes linked to rare discovery in medical breakthrough
A landmark study has found 69 previously unidentified genetic determinants of rare disease, including uncommon forms of ...
Technology Networks5 天
69 New Genetic Causes of Rare Diseases Identified
A study using Genomics England’s 100,000 Genomes Project identified 69 new genetic variants linked to rare diseases, ...
Mirage News6 天
Sheffield Team Unveils New Genes Tied to Rare Diseases
A landmark study has found 69 previously unidentified genetic determinants of rare disease, including uncommon forms of ...
The University of Sheffield6 天
Sheffield researchers help discover previously unidentified genes linked to rare diseases
A landmark study has found 69 previously unidentified genetic determinants of rare disease, including uncommon forms of ...