usz.ch Background: Duchenne muscular dystrophy (DMD) leads to progressive impairment of muscle function ... a family history consistent with X chromosome linked recessive inheritance.16 Information on ...

This status is awarded by the… Capricor Therapeutics has completed its submission of a biologics license application (BLA) seeking U.S. approval of deramiocel, the company’s cell therapy for heart ...

Daily supplementation of beta-hydroxy-beta-methylbutyrate (HMB) could improve overall daily activity in Duchenne muscular dystrophy (DMD), a study found.

Santhera Pharmaceuticals will launch its new drug for Duchenne muscular dystrophy in the UK within the next few weeks, after getting confirmation it will be covered by the NHS in all four nations.

The announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...

Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...

Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as Spinal Muscular Atrophy (SMA) and Duchenne Muscular Dystrophy (DMD).

Leber congenital amaurosis (LCA) and early-onset severe retinal dystrophy (EOSRD) are both genetically and phenotypically heterogeneous, and characterised clinically by severe congenital/early infancy ...

Amid the uproar over the firing of 18 inspectors general, a report offering a coda to the aducanumab approval episode has ...

The rate of tax to be paid varies depending on what is left to the individual. As is the case more broadly, the more inherited, the more tax. Inheritance is only taxed if the individual who died was ...