Dublin, Jan. 31, 2025 (GLOBE NEWSWIRE) -- The "Thalassemia Market by Treatment Type, by Type, by Distribution Channel, and by Region" report has been added to ResearchAndMarkets.com's offering.
Yoltech Therapeutics Co. Ltd. has advanced YOLT-204 into the clinic for the treatment of transfusion-dependent β-thalassemia (TDT). If successful, YOLT-204 may provide an off-the-shelf curative ...
One sickle cell patient told ITV News the new gene therapy being rolled out for use on the NHS means they "finally have something to look towards". | ITV National News ...
Thalassemia patients, who suffer from chronic anemia and risk severe complications, currently have limited treatment options. PYRUKYND, if approved, would offer a disease-modifying oral medication ...
Thalassemia is a congenital blood disorder ... and poor adherence to treatment increases the risk of complications and shortens survival. Patient adherence practices are generally seen as a ...
Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with NHS England for eligible sickle cell disease (SCD) patients to access the CRISPR/Cas9 gene-edited therapy, CASGEVY® ...