Contract Pharma4 天
ENCell’s EN001 Granted Orphan Drug Designation by FDA
ENCell’s investigational drug EN001 has been granted Orphan Drug Designation by the FDA for the treatment of ...
Business Wire4 天
ENCell’s EN001 Receives Orphan Drug Designation from the U.S. FDA for Charcot-Marie-Tooth ...
EN001, a novel therapy under development by ENCell, has been granted Orphan Drug Designation by the U.S. FDA for the treatment of Charcot-Marie-Tooth (CMT) disease. Phase 1 clinical trial confirmed ...
Claiborne Progress5 天
TN House of Representatives weekly wrap
By State Rep. Dennis Powers House advances bill to regulate hemp-derived THC products To protect consumer health and safety, a new law seeks to regulate the sale and distribution of hemp-derived ...
Sheffield researchers help identify genes linked to rare discovery in medical breakthrough
A landmark study has found 69 previously unidentified genetic determinants of rare disease, including uncommon forms of ...
Mirage News5 天
Sheffield Team Unveils New Genes Tied to Rare Diseases
A landmark study has found 69 previously unidentified genetic determinants of rare disease, including uncommon forms of ...
The University of Sheffield6 天
Sheffield researchers help discover previously unidentified genes linked to rare diseases
A landmark study has found 69 previously unidentified genetic determinants of rare disease, including uncommon forms of ...
Chattanoogan.com10 天Opinion
Capitol Report From State Rep. Greg Vital For Feb. 28
The Tennessee House of Representatives on Feb. 27 unanimously passed a resolution urging the Tennessee Department of Health ...
Centralising genomic data crucial for recruitment in rare disease trials
Rare disease patients can only benefit from research if they can be contacted about ongoing clinical trials, an expert says.
Become A Certified CMT-FOM Clinical Evaluator At The HNF Clinical Trial Readiness Summit
Become one of the first Fully Certified CMT-FOM Clinical Evaluators at the upcoming HNF Clinical Trial Readiness Summit in Nashvil ...
Queen Mary University of London11 天
Landmark study finds 69 previously unidentified genetic determinants of rare disease
Importantly, the strongest overall genetic and experimental evidence supported the newly-discovered genetic variants for rare ...
Mirage News11 天
Research Uncovers 69 New Genetic Links to Rare Disease
Rare diseases collectively affect between 4% and 6% of individuals worldwide. Despite advances in genetic testing, the lack ...
KED Global11 天
Chong Kun Dang to build new plant for foray into biologics market
Chong Kun Dang Pharmaceutical Corp. is discussing building a research center and a plant in Siheung, about 30 kilometers southwest of Seoul, with the Siheung c ...