HDBuzz reported live updates on Bluesky from the 2025 HD Therapeutics Conference. Read on for coverage of Day 1. #CHDI2025 ...

Huntington’s disease is an inherited neurological disorder causing movement, cognitive, and behavioral issues. Effective ...

Feb. 11, 2025 — Over 1,000 genes may serve as possible treatment targets for individuals with kidney disease, according to a new study. By creating the most complete and detailed genetic 'map ...

A new discovery offers hope for Huntington’s disease. This discovery provides hope that a DNA repair process may help slow or ...

But the voices represent a vast improvement on previous communication technologies and are already improving the lives of people with motor neuron diseases, says Richard Cave, a speech and ...

RNA therapeutics is rapidly transforming the landscape of drug discovery, offering groundbreaking treatments for rare diseases and beyond. Advances in mRNA and RNA-targeting technologies have made ...

Huntington's disease (HD) is an autosomal dominant neurodegenerative disorder caused by a polyglutamine repeat expansion within the huntingtin protein. HD is characterized by problems with ...

Credit: Manjurul via Getty Images. The CRISPR-based gene therapy Casgevy (exagamglogene autotemcel) has been made available to patients with sickle cell disease in England, following positive guidance ...

Australian cancer researchers are the first to establish a next-generation gene-editing tool for modeling and interrogating human disease. A novel pre-clinical model expressing an enhanced version ...